Join us in celebrating Rare Disease Month the entire month of February, leading up to Rare Disease Day on February 28.

• Follow our social media posts throughout the month

• Share our social media posts with your family and friends

• Share your Rare Disease story HERE

Mark your calendars for UCD Awareness Month this April!
More information coming soon.

Save the date for the 2026 NUCDF Family Conference. The event will take place July 17-19 in Memphis, TN. Registration will open soon.

Representatives from the University of California, Los Angeles (UCLA) are working toward a potential one-time gene therapy treatment for Arginase Deficiency and have seen promising results in early research models.

While there are still important steps ahead—including FDA review and funding—they want to make sure the voices of individuals and families affected by Arginase Deficiency are heard.

ARG-1 families, you're invited to take a 15-20 minute anonymous survey. The survey will gather your experiences, perspectives, and thoughts on gene therapy, to help strengthen the data and support progress for the ARG-1 community.